Clinical Trials

Angelman syndrome

Displaying 2 studies

A Study To Investigate The Safety, Tolerability, Pharmacokinetics And Pharmacodynamics Of RO7248824 In Participants With Angelman Syndrome Rochester, MN

The primary objective of this study is to investigate the safety and tolerability of RO7248824 in participants with Angelman Syndrome (AS) aged 1-12 years.
A Study to Establish a Patient Clinical and Genetic Information Database to Better Characterize Symptoms and Causes of Angelman Syndrome Rochester, MN

The purpose of this study is to establish a patient and clinical information database, and a genetic material biobank to better characterize the symptoms and unknown genetic causes of Angelman syndrome