A Study to Test the Efficacy, Safety, and Pharmacokinetics of Rozanolixizumab in Adult Study Participants With Leucine-Rich Glioma Inactivated 1 Autoimmune Encephalitis

Overview

About this study

The purpose of the study is to assess the efficacy of rozanolixizumab as measured by seizure freedom, change in cognitive function, use of rescue medication, onset of seizure freedom and to assess safety and tolerability.

Participation eligibility

Participant eligibility includes age, gender, type and stage of disease, and previous treatments or health concerns. Guidelines differ from study to study, and identify who can or cannot participate. There is no guarantee that every individual who qualifies and wants to participate in a trial will be enrolled. Contact the study team to discuss study eligibility and potential participation.

Inclusion Criteria:

- Study participant must be ≥ 18 to ≤ 89 years of age

- Study participant must be seropositive for leucine-rich glioma inactivated 1 (LGI1)
antibody

- Study participant must have ≥ 2 seizures/week during the Screening Period or have experienced such seizures that stopped following high dose corticosteroids (500 to 1000 milligram (mg) methylprednisolone (MP) equivalent/day):

- Either faciobrachial dystonic seizures (FBDS) with or without other focal (partial) seizures including focal to bilateral tonic clonic

- Or focal (partial) seizures including focal to bilateral tonic clonic and fulfil the following new-onset Autoimmune encephalitis (AIE) criteria

- Study participant has initiated or re-initiated corticosteroids at a dose of 500 to 1000 mg MP equivalent/day within 42 days prior to randomization. Participants re-initiating corticosteroids are eligible only if re-initiation is due to seizure rebound and within the timeframe outlined. If the study participant has initiated a steroid taper, the study participant cannot receive an oral steroid dose lower than
40mg/day when randomized

- Study participant with onset of disease symptom between 0 to 12 months prior to Screening, per investigator's assessment.

- Study participant weighs at least 35 kg at Screening

- A female participant is eligible to participate if she is not pregnant, not breastfeeding, and at least one of the following conditions applies:

i) Not a woman of childbearing potential (WOCBP) OR ii) A WOCBP who agrees to follow the contraceptive guidance during the treatment period and for at least 90 days after
the final dose of study treatment

Exclusion Criteria:

- Study participant has a known hypersensitivity to any components of the study medication or any other anti-neonatal Fc receptor (FcRn) medications.

- Study participant has a confirmed prior diagnosis of epilepsy or new onset seizures that are unrelated to LGI1 autoimmune encephalitis (AIE) or has any known or suspected medical cause for the onset of seizures other than possible AIE

- Study participant has a known active neoplastic disease or history of neoplastic disease within 5 years of study entry

- Study participant has renal impairment, defined as glomerular filtration rate (GFR) < 30mL/min/1.73m^2 at the Screening Visit

- Study participant has a clinically important active infection (including unresolved or not adequately treated infection) as assessed by investigator, including participants with a serious infection within 6 weeks prior to the first dose of IMP.

- Study participant has a history of chronic ongoing infections

- Study participant has 12-lead ECG with findings considered clinically significant by the investigator.

- Study participant has current unstable liver or biliary disease, per investigator assessment, defined by the presence of ascites, encephalopathy, coagulopathy,
hypoalbuminemia, esophageal or gastric varices, persistent jaundice, or cirrhosis

- . Study participant has positive TB test at the Screening Visit unless it is determined by a TB specialist that the positive result is related to an adequately treated latent TB infection

- Study participants met any of the following TB exclusion criteria: − Known active TB disease − History of active TB involving any organ system unless adequately treated according to World Health Organization (WHO)/US Center for Disease Control therapeutic guidance and proven to be fully recovered upon consult with a TB specialist − Latent tuberculosis infection (LTBI) (unless appropriate prophylaxis is initiated at least 4 weeks prior to IMP dosing and will be continued to completion of prophylaxis). Prophylaxis should be in accordance with applicable clinical guidelines and TB specialist judgment based on the origin of infection

− High risk of exposure to TB infection, as assessed by the investigator

− Current nontuberculous mycobacterial (NTM) infection or history of NTM infection unless proven to be fully recovered.

- . Study participant has a current or medical history of IgA deficiency

- Study participant has a history of solid organ transplant or hematopoietic stem cell transplant

- Study participant has undergone a splenectomy

- Study participant has a current or medical history of primary immune deficiency

- Study participant has received a live vaccination within 4 weeks prior to the Baseline Visit; or intends to have a live vaccination during the course of the study or within 8 weeks following the final dose of investigational medicinal product (IMP)

- Study participant has previously received rozanolixizumab drug product

- Alanine transaminase (ALT), aspartate aminotransferase (AST), or alkaline phosphatase (ALP) are > 3x upper limit of normal (ULN)

- Study participant has a total IgG level ≤ 5.5 g/L at the Screening Visit

- Study participant has absolute neutrophil count < 1500 cells/mm^3 at the Screening Visit

Note: Other protocol defined Inclusion/Exclusion Criteria may apply.

Eligibility last updated 1/4/24. Questions regarding updates should be directed to the study team contact.

Participating Mayo Clinic locations

Study statuses change often. Please contact the study team for the most up-to-date information regarding possible participation.

Mayo Clinic Location Status

Rochester, Minn.

Mayo Clinic principal investigator

Divyanshu Dubey, M.B.B.S.

Closed for enrollment

Jacksonville, Fla.

Mayo Clinic principal investigator

Alfonso Lopez Chiriboga, M.D.

Closed for enrollment

Scottsdale/Phoenix, Ariz.

Mayo Clinic principal investigator

Nicholas Zalewski, M.D.

Closed for enrollment

More information

Publications

Publications are currently not available
.
CLS-20540753

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